Latest Articles

Factor VIII Activity Assays - A Guide to PK Testing

Pharmacokinetic (PK) testing with accurate Factor VIII assays may help personalize hemophilia A treatment.^1,2 This article reviews one-stage and chromogenic methods and their clinical use.

How ASMD Can Impact Quality of Life and Average Life Expectancy​

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How to Differentiate Gaucher Disease Type 1

The Spectrum of Gaucher Disease Symptoms

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ASMD Inheritance Patterns in Families

Hear from Healthcare Providers About Their Experience Managing Patients with ASMD